1.Weinberg, M.S., R.J. Samulski, and T.J. McCown, Adeno-associated virus (AAV) gene therapy for neurological disease. Neuropharmacology, 2013. 69: p. 82-8.
2.Iwata, N., et al., Global brain delivery of neprilysin gene by intravascular administration of AAV vector in mice. Sci Rep, 2013. 3: p. 1472.
3.Pang, J.J., et al., Comparative analysis of in vivo and in vitro AAV vector transduction in the neonatal mouse retina: effects of serotype and site of administration. Vision Res, 2008. 48(3): p. 377-85.
4.Lisowski, L., et al., Selection and evaluation of clinically relevant AAV variants in a xenograft liver model. Nature, 2014. 506(7488): p. 382-6.
5.Wang, L., et al., Sustained expression of therapeutic level of factor IX in hemophilia B dogs by AAV-mediated gene therapy in liver. Mol Ther, 2000. 1(2): p. 154-8.
6.Nathwani, A.C., et al., Safe and efficient transduction of the liver after peripheral vein infusion of self-complementary AAV vector results in stable therapeutic expression of human FIX in nonhuman primates. Blood, 2007. 109(4): p. 1414-21.
7.Manno, C.S., et al., Successful transduction of liver in hemophilia by AAV-Factor IX and limitations imposed by the host immune response. Nat Med, 2006. 12(3): p. 342-7.
8.Palomeque, J., et al., Efficiency of eight different AAV serotypes in transducing rat myocardium in vivo. Gene therapy, 2007. 14(13): p. 989-997.
9.Vassalli, G., et al., Adeno-associated virus (AAV) vectors achieve prolonged transgene expression in mouse myocardium and arteries in vivo: a comparative study with adenovirus vectors. International Journal of Cardiology, 2003. 90(2-3): p. 229-238.
10.Bish, L.T., et al., Adeno-associated virus (AAV) serotype 9 provides global cardiac gene transfer superior to AAV1, AAV6, AAV7, and AAV8 in the mouse and rat. Human gene therapy, 2008. 19(12): p. 1359-1368.
11.Halbert, C.L., et al., Repeat transduction in the mouse lung by using adeno-associated virus vectors with different serotypes. Journal of virology, 2000. 74(3): p. 1524-1532.
12.Takeda, S., et al., Successful gene transfer using adeno-associated virus vectors into the kidney: comparison among adeno-associated virus serotype 1-5 vectors in vitro and in vivo. Nephron Exp Nephrol, 2004. 96(4): p. e119-26.
13.Qi, Y.F., et al., Comparison of the transduction efficiency of tyrosine-mutant adeno-associated virus serotype vectors in kidney. Clin Exp Pharmacol Physiol, 2013. 40(1): p. 53-5.
14.The potent dial of adeno-assoc iated viral vectors for gene delivery to muscle tissue. Expert Opin Drug Deliv., 2014. 11(3)。
15.Z Wang1, H.-I.M., 3, J Li1, L Sun1, J Zhang1 and X Xiao1,2, Rapid and highly efficient transduction by doublestranded adeno-associated virus vectors in vitro and in vivo. Gene Therapy, 2003. 2003(10): p. 2105—2111.
16.Polyak, Steven, et al. “Gene delivery to intestinal epithelial cells in vitro and in vivo with recombinant adeno-associated virus types 1, 2 and 5.” Digestive diseases and sciences 53.5 (2008): 1261-1270.
17.Polyak, S., et al., Gene delivery to intestinal epithelial cells in vitro and in vivo with recombinant adeno-associated virus types 1, 2 and 5. Digestive diseases and sciences, 2008. 53(5): p. 1261-1270.